40597-87-3Relevant articles and documents
COMPOUNDS FOR IMPROVING MRNA SPLICING
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Page/Page column 219, (2016/08/10)
Provided herein are compounds useful for improving mRNA splicing in a cell. Exemplary compounds provided herein are useful for improving mRNA splicing in genes comprising at least one exon ending in the nucleotide sequence CAA. Methods for preparing the compounds and methods of treating diseases of the central nervous system are also provided.