1044243-54-0Relevant academic research and scientific papers
EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
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, (2020/01/08)
Antisense oligomers and antisense oligomer conjugates complementary to a selected target site in the human dystrophin gene to induce exon 53 skipping are described.
COMPOSITIONS AND METHODS FOR TREATING DUCHENNE MUSCULAR DYSTROPHY AND RELATED DISORDERS
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, (2017/05/14)
The present disclosure relates to compositions and methods for the treatment of Duchenne muscular dystrophy and related disorders. Modified antisense oligomers are disclosed for the treatment of Duchenne muscular dystrophy and related disorders.
EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
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, (2016/05/02)
Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 53 skipping are described.
