PO
5mpk
4.8
35
NA
3.0
NA
These optimized inhibitors generally demonstrate fair to good kinase selectivity. For instance, only three off-target kinases [Abl,
Musk and RAF (Y340D, Y341D)] of the 65 tested, were inhibited >50% by hydroxypyridine 6d at 1 µM.14 When (S, S)-13b was
tested in the same panel at 0.1 µM, eight off-target kinases were inhibited with >50% (Abl, CDK2, CK1α, Flt3, KDR, PAK4, Txk,
YES). We believe that 6d is more selective than 13b because of interaction between the hydroxyl group of 6d and the unique
Ser442 of ITK.
In summary, we have discovered a new class of benzothiazole-based ITK inhibitors and were able to improve the potency by
920-fold from a HTS hit through rational design. We were able to elucidate the binding mode of these inhibitors by solving the X-
ray crystal structures of representative analogs complexed to the kinase domain of ITK. Advanced leads such as 13b and (S, S)-19,
possesses sub-nanomolar inhibitory potency, double-digit nanomolar cell potency, triple-digit micromolar aqueous solubility and
good selectivity over LCK.
References & Notes
1.
Felices, M,; Falk, M.; Kosaka, Y.; Berg, L.J. Adv. Immunol. 2007, 93, 145.
2. Sakaguchi, S.; Benham, H.; Cope, A.P.; Thomas R.; Immunol. Cell Biol.; 2012, 90, 277
3. Mueller, C.; August, A. J. Immunol.2003, 170, 5056.
4.
Schaeffer, E. M.; Debnath, J.; Yap, G.; McVicar, D.; Liao, X. C.; Littman, D. R.;Sher, A.; Varmus, H. E.; Lenardo, M. J.; Schwartzberg, P. L.
Science 1999, 284, 638.
5.
For small-molecule inhibitors of ITK, see (a) Das, J.; Liu, C.; Moquin, R.V.; Lin, J.; Furch, J. A.; Spergel, S. H.; McIntyre, K. W.; Shuster, D. J.;
O’Day, K. D.; Penhallow, B.; Huang, C-Y.; Kanner, S. B.; Lin, T-A.; Dodd, J. H.; Barrish, J. C.; Wityak, J. Bioorg. Med. Chem. Lett. 2006,16,
2411; (b) Lin, T. A.; McIntyre, K..; Das, J.; Liu, C.; O’Day, K. D.; Penhallow, C-Y.; Whitney, G. S.; Shuster, D. J.; Xia, X.; Towsend, R.;
Postelnek, J.; Spergel, S. H.; Lin, J.; Moquin, R. V.; Furch, J. A.; Kamath, A. V.; zhang, H.; Marathe, P. H.; Perez-Villar, J. J.; Doweyko, A.;
Killar, L.; Dodd, J. H.; Barrish, J. C.; Wityak, J.; Kanner, S. B. Biochem. 2004, 43, 11056; (c) Snow, R.J.; Abeywardane. A.; Campbell , S.;
Lord, J.; Kashem, M. A.; Khine, H. H.; King, J.; Kowalski, J. A.; Pullen, S. S.; Roma, T.; Roth, G. P.; Sarko, C. R.; Wilson, N. S.; Winter, M. P.;
Wolak, J. P.; Cywin, C. L. Bioorg. Med. Chem. Lett. 2007, 17, 3660; (d) Moriarty, K. J.; Winters M, Qiao, L.; Ryan, D.; DesJarlis, R.; Robinson,
D.; Cook, B. N.; Kashen, M. A.; Kaplita, P. V.; Liu, L. H.; Farrell, T. M.; Khine, H. H.; King, J.; Pullen, S. S.; Roth, G. P.; Magolda, R.
Takahashi, H. Bioorg. Med. Chem. Lett. 2008,18, 5537; (e) Winters, M.P.; Robinson, D. J.; Khine, H. H.; Pullen, S. S; Woska Jr.; J. R.;
Raymond, E. L.; Sellati, R.; Cywin, C. L.; Snow, R. J.; Kashem, M. A.; Wolak, J. P.; King, J.; Kaplita, P. V.; Liu., L. H.; Bioorg. Med. Chem.
Lett. 2008, 18, 5541; (f) Riether, D.; Zindell. R.; Kowalski A, et al. Bioorg. Med. Chem. Lett. 2009, 19,1588; (g) Lo H.Y.; Bentzien, J.; Fleck, R.
W.; Pullen, S. S.; Khine, H. H.; Woska, J. R.; Kugler, S. Z.; Kashen, M. A.; Takahashi, H. Bioorg. Med. Chem. Lett. 2008, 18, 6218; (h)
Charrier, J. D.;Miller, A.;Kay, D. P.;Brenchley, G.;Twin, H. C.;Collier, P. N.;Ramaya, S.;Keily, S. B.;Durrant, S. J.;Knegtel, R. M.;Tanner, A.
J.;Brown, K.; Curnock, A. P.;Jimenez, J. M. J. Med.Chem. 2011, 54, 2341; (i) Herdemann. M.; Weber, A.; Jonveaux, J; Jonveaux, J.; Schwoebel,
S.; Heit, I. Bioorg. Med. Chem. Lett. 2011, 21, 1852; (j) McLean, L. R.; Zhang, Y.; Zaidi, N.; Bi, X.; Wang, R.; Dharanipragada, R.; Jurcak, J.
G.; Gillespy, T. A.; Zhao, Z.; Musick, K. Y.; Choi, Y. M.; Barrague, M.; Peppard, J.; Smicker, M.; Duguid, M.; Parkar, A.; Fordham, J.;
Kominos, D. Bioorg. Med. Chem. Lett. 2012, 22, 3296; (k) Zapf, C. W.;Gerstenberger, B. S.;Xing, L.;Limburg, D. C.;Anderson, D. R.;Caspers,
N.;Han, S.;Aulabaugh, A.; Kurumbail, R.;Shakya, S.;Li, X.;Spaulding, V.;Czerwinski, R. M.;Seth, N.;Medley, Q. G. J. Med. Chem., 2012, 55,
10047. (l) For a recent review on ITK inhibitors, see: Charrier, J-D.; Knegtel, R. MA. Expert Opin. Drug Discov. 2013, 8, 369.
Newcomb, M.; Choi S, Toy, P.H. Can. J. Chem. 1999, 77, 1123.
6.
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Hamdouchi, C.; Topolski, M.; Goedkin, V.; Walborsky, H. M. J. Org. Chem. 1993, 58, 3148.
Biedeger, R.J.; Decker, R.E.; Dupre, B.; Hamaker, L.K.; Holland, G.W.; Kassir, J.M.; Li, W.; Market, R.V.; Nguyen, N.; Scott, I. L.; Wu, C.
European Patent: EP 1213288 A1, 2002.
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(a) Brown, K; Long, J.M.; Vial, S.C.M.; Dedi, N.; Dunster, N.J.; Renwick, S.B.; Tanner, A.J.; Frantz, J.D.; Fleming, M.A.; Cheetham, G.M.T.;
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10. Biochemical assay: GST-ITK full length enzyme was from Invitrogen (PV3875) and substrate was BLK peptide (Ac-EFPIYDFLPAKKK-NH2).
Reactions were carried out in a final volume of 51 µl with 50 mM HEPES (pH 7.2), 15 mM MgCl2, 2 mM DTT, 0.015% Brij-35, 1 nM ITK, 2µM
substrate, 20 µM ATP, and 2% DMSO. After 35 min incubation at RT, reactions were stopped upon addition of 10 µl of 30% TCA. Samples
were centrifuged (4350 rpm, 4 °C, 5 min) and subjected to LC/MS analysis on a Waters Acquity UPLC/TQD system equipped with a Waters
Acquity UPLC BEH C18 (2.1 × 50 mm) 1.7 µm column (injection volume: 5 µl, column temperature: 60 °C, flow rate: 1 ml/min, solvent A:
0.1% formic acid in LC/MS grade water, solvent B: 0.1% formic acid in LC/MS grade ACN). Analytes were separated by applying a gradient
from 15 to 32% solvent B within 0.7 min and detected in positive mode ESI-MS/MS by MRM (multiple reaction monitoring) of transitions
819.8/84.8 (BLK substrate) and 859.0/84.8 as well as 859.0/120.7 (phosphorylated BLK product).
11. The ability of compounds to inhibit phosphorylation of PLCg1 in Jurkat cells was determined using an immuno-detection assay that will be
described in detail in a separate communication.
12. Ishikawa, M.; Hashimoto, Y. J. Med. Chem. 2011, 54, 1539.
13. (a) For a benzothiazole-based LCK inhibitor, see Das, J.; Lin, J.; Moquin, R. V.; Shen, Z.; Spergel,S. H.; Wityak, J.; Doweyko, A. M.; DeFex, H.
F.; Fang, Q.; Pang, S.; Pitt, S.; Shen, D. R.; Schieven, G. L.; J. C. Barrish. Bioorg. Med. Chem. Lett. 2003, 13,2145; (b) We did not have in-house
X-ray crystal structure of LCK, so do not have structure-based explanation of selectivity over LCK.
14. Selectivity screening was performed by SelectScreen® Kinase Profiling Services (Invitrogen-Life Technologies, Madison, USA).